Survival analysis of haematopoietic cell transplantation for childhood cerebral X-linked adrenoleukodystrophy: a comparison study.

TitleSurvival analysis of haematopoietic cell transplantation for childhood cerebral X-linked adrenoleukodystrophy: a comparison study.
Publication TypeJournal Article
Year of Publication2007
AuthorsMahmood A, Raymond GV, Dubey P, Peters C, Moser HW
JournalLancet neurology
Volume6
Issue8
Pagination687-92
Date Published2007 Aug
Abstract

Favourable outcomes have been reported for patients with childhood cerebral adrenoleukodystrophy (CCALD) who had received haematopoietic cell transplantation (HCT) at the early stage of cerebral involvement. However, comparative data for non-transplanted CCALD patients are limited. We analysed survival of CCALD patients who had not received HCT and, in a subgroup with early cerebral disease, compared survival in those who underwent HCT with those who did not.

Alternate JournalLancet Neurol